FSU | Florida Institute for Pediatric Rare Diseases

FLORIDA STATE UNIVERSITY

The official logo for the Florida Institute for Pediatric Rare Diseases at the FSU College of Medicine. The design features the classic "FSU" block lettering separated by a vertical line from the institute's name in garnet text.
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2024 News

2024 News & Events

IPRD RESEARCHERS

Highlights a collaborative academic or professional environment with Irianto lab members with "DEC. 19" text.

Jerome Irianto Lab Shares Research Updates on Pediatric Glioblastoma

(Dec. 19, 2024)
Diagram of green dyed AAVs

“Metabolic engineering improves transduction efficiency and downstream vector isolation by altering the lipid composition of extracellular vesicle-enclosed AAV”

Elizabeth D. Wasson, B.S.; Deirdre M. McCarthy, B.Sc.; Pradeep G. Bhide, Ph.D.
(Dec. 12, 2024)

A group of ten researchers is shown on stage, following a scientific conference.

FSU’s International Genetically Engineered Machine team wins gold in Paris for rare disease research

(Nov. 19, 2024)

A researcher is shown giving a formal presentation.

Akash Gunjan Lab Shares Research Updates on Pediatric High-Grade Glioblastoma 

(Oct. 31, 2024)

Researchers are seen in a lab or office environment discussing project strategies.

Cesar Rodriguez Lab Shares Research Updates on Fish odor syndrome

(Oct. 17, 2024)

A researcher is shown at his desk with a dual-monitor setup, featuring a video call and coding on a laptop, indicating the early stages of data processing or project coordination.

Cesar Rodriguez Lab Shares Research Updates on AI Knowledge Hub 

(Oct. 13, 2024)

Four female researchers standing in a laboratory. A maroon box in the top-left corner features the text "SEPT. 19" in white.

Deirdre McCarthy Lab Shares Research Updates on Tay-Sachs Disease

(Sept. 19, 2024)

“Behavioral, neurotransmitter and transcriptomic analyses in male and female Fmr1 KO mice” 

Deirdre M. McCarthy, B.Sc.; Cynthia Vied, Ph.D.; Yuan Wang, Ph.D.; Pradeep G. Bhide, Ph.D.
(Sept. 5, 2024)

Dr. Chelko's lab group photo

Stephen Chelko Lab Shares Research Updates on Arrythmogenic Cardiomyopathy 

(Aug. 30, 2024)

Diagram of pediatric brain tumor cells with text "AUG 12."

“Feeder-free differentiation of human iPSCs into natural killer cells  with cytotoxic potential against malignant brain rhabdoid  tumor cells”

Sonia Kiran, B.S.; Yu Xue, B.S.; Drishty B. Sarker, B.S.; Qing-Xiang Amy Sang, Ph.D.
(Aug. 12, 2024)

Initial team portraits in the laboratory signify the early stages of group assembly and protocol establishment.

Yi Zhou Lab Shares Research Updates on Developmental and Epileptic Encephalopathies 

(Aug. 12, 2024)

RARE DISEASE NEWS

Brain scan diagram with the text "OCT 23"

Broad scientists identify an ultrarare disease caused by a mutation in CHASERR IncRNA, a long non-coding RNA 

(Oct. 23, 2024)

Dean Littles speaking at an FSU event with text "OCT 7"

New FSU Institute researching Rare Pediatric Diseases 

(Oct. 7, 2024)

A group of legislators unveiling five million dollar check for IPRD with the text "OCT 7"

FSU Discovery Days launch includes $5 million check to fund pediatric rare disease research

(Oct. 7, 2024)

A close-up of a DNA double helix model with a gloved hand using silver tweezers to manipulate a specific gene segment. A maroon box in the top-left corner features the text "JUNE 20" in white.

Zatolmilast an experimental drug brings new hope for Fragile X patients 

(Sept. 23, 2024)

Adam Anderson family photo with the text "AUG 12"

Lawmaker giving hope to kids with rare diseases after losing his 4-year-old son 

(Aug. 16, 2024)

A 3D illustration shows a gloved hand using silver tweezers to carefully insert or remove a small, pink segment from a DNA double helix model. A maroon box in the top-left corner displays the text "JUNE 20" in white.

FDA Expands Approval of Gene Therapy for Patients with Duchenne Muscular Dystrophy 

(June 20, 2024)

A three-torch sculpture sits atop a brick fountain, with the Florida State University seal and campus buildings in the background. A maroon box in the top-left corner displays the text "JUNE 13" in white.

Florida State University looks to continue momentum with vital state funding

(June 13, 2024)

Adam Anderson speaking at Florida capitol with the text "FEB 1."

FSU Launches groundbreaking Institute for Pediatric Rare Diseases

(Feb. 1, 2024)

EVENTS

Discovery Days speakers on stage with the text "OCT 7"

Discovery Days Pediatric Rare Disease Symposium

(Oct. 7, 2025)

TIMELINE

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